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MyoAAV-delivered sup-tRNA increases full-length dystrophin expression
Xiuyi Ai, Yue Chang, Ruo Wu, Jie Liu, Pei Zhang, Yayu Wang, Zhuoyin Zheng, Shu Zhang, Yongchang Chen, Shiwen Wu
https://doi.org/10.1016/j.gendis.2025.101666
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5
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Genes & Diseases
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May 01, 2025